CRISPR Breakthrough Brings First In-Body Cure With Lonvo-Z

A CRISPR Therapy Just Cured A Disease From Inside The Body For The First Time. The Gene-Editing Era Officially Started Monday ...
Los Angeles Times

How CRISPR Works: Unpacking the Science of Cas9 and Gene Modification

CRISPR functions as a programmable genetic memory system derived from bacterial immune defenses against viral infections. Guide RNA allows for rapid multiplexed targeting compared to older ...
Oncology Nurse Advisor

First Patient Dosed in AVC-203 Study for R/R B-Cell Malignancies, ALL

By using CRISPR/Cas9 to engineer cells from healthy donors, AVC-203 is designed to circumvent graft-versus-host disease and host-mediated rejection.
The Peninsula Qatar

Sidra Medicine introduces Qatar’s first advanced gene-editing therapy for sickle cell disease and thalassemia

Sidra Medicine, a member of Qatar Foundation, has been qualified by Vertex Pharmaceuticals as one of a of a limited number of ...
Morning Overview on MSN

Compact CRISPR tool boosts in-body gene editing to 90% in lab tests

For the millions of people living with genetic diseases like muscular dystrophy and inherited liver disorders, one of the ...
University of California

Novel gene therapy trial for sickle cell disease launches

UCSF Benioff Children’s Hospital Oakland is enrolling patients in an innovative clinical trial that seeks to cure sickle cell disease. The trial is the first in the U.S. to apply non-viral CRISPR-Cas9 ...
C&EN

The Power to Edit DNA: CRISPR-Cas9 and Sickle Cell Disease

In December 2020, the New England Journal of Medicine published a paper titled CRISPR-Cas9 Gene Editing for Sickle Cell Disease and β-Thalassemia, marking an exciting new chapter in the treatment of ...