Aplastic anemia is a rare, life-threatening blood disorder where patients are unable to make enough blood cells due to the immune system's attack on blood stem cells. The condition can progress to ...

Doctors stumbled upon a type rarer than “golden blood”—and suspect more patients carry the bizarre genetic anomaly.

Researchers have used saturation genome editing to test every variant in the non coding gene RNU4 2, revealing new pathogenic ...

Before Baby KJ was six months old, doctors at Children’s Hospital of Philadelphia injected a gene-editing therapy built for ...

Dogs come in a variety of coat colors, but some can look a lot more unique than others! Check out these 15 dogs with ...

Readout to Include One-Year Cohort 1 Results and Early Cohort 2 Data; Webcast Conference Call Planned to Review RIDGE-1 Data at ASGCT Additional ...

Researchers are uncovering how X chromosome inactivation and Xi expressed genes may contribute to autism’s sex bias, offering ...

J. Craig Venter, a pioneering scientist who helped produce the first draft of the human genome, has died at 79.

SINGAPORE, PARIS and PHILADELPHIA, April 28, 2026 /PRNewswire/ -- Nuevocor, a clinical-stage biotechnology company developing novel therapies for patients suffering from life-threatening ...